Diseases which can currently be treated with Stem Cells Therapy
Leukemias (all therapies are allogeneic)
(Leukemia is a cancer of the blood immune system, whose cells are called leukocytes or white cells)
Acute Leukemia
Acute Lymphoblastic Leukemia (ALL)
Acute Myelogenous Leukemia (AML)
Acute Biphenotypic Leukemia
Acute Undifferentiated Leukemia
Chronic Leukemia
Chronic Myelogenous Leukemia (CML)
Chronic Lymphocytic Leukemia (CLL)
Juvenile Chronic Myelogenous Leukemia (JCML)
Juvenile Myelomonocytic Leukemia (JMML)
Myelodysplastic Syndromes – (pre-leukemia)
Refractory Anemia (RA)
Refractory Anemia with Ringed Sideroblasts (RARS)
Refractory Anemia with Excess Blasts (RAEB)
Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
Chronic Myelomonocytic Leukemia (CMML)
Lymphomas (all therapies are allogeneic)
(Lymphoma is a cancer of the leukocytes that circulate in the blood and lymph vessels)
Hodgkin’s Lymphoma
Non-Hodgkin’s Lymphoma (Burkitt’s Lymphoma)
Other Disorders of Blood Cell Proliferation (all therapies are allogeneic)
Anemias (Anemias are deficiencies or malformations of red cells)
Aplastic Anemia
Congenital Dyserythropoietic Anemia
Fanconi Anemia (Note: the first cord blood transplant in 1988 was for FA, an inherited disorder)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pure Red Cell Aplasia
Inherited Red Cell Abnormalities
Beta Thalassemia Major (also known as Cooley’s Anemia)
Blackfan-Diamond Anemia
Pure Red Cell Aplasia
Sickle Cell Disease
Inherited Platelet Abnormalities
Amegakaryocytosis / Congenital Thrombocytopenia
Glanzmann Thrombasthenia
Inherited Immune System Disorders – Severe Combined Immunodeficiency (SCID)
SCID with Adenosine Deaminase Deficiency (ADA-SCID)
SCID which is X-linked
SCID with absence of T & B Cells
SCID with absence of T Cells, Normal B Cells
Omenn Syndrome
Inherited Immune System Disorders – Neutropenias
Kostmann Syndrome
Myelokathexis
Inherited Immune System Disorders – Other
Ataxia-Telangiectasia
Bare Lymphocyte Syndrome
Common Variable Immunodeficiency
DiGeorge Syndrome
Hemophagocytic Lymphohistiocytosis
Leukocyte Adhesion Deficiency
Lymphoproliferative Disorders (LPD)
Lymphoproliferative Disorder, X-linked (also known as Epstein-Barr Virus Susceptibility)
Wiskott-Aldrich Syndrome
Myeloproliferative Disorders
Acute Myelofibrosis
Agnogenic Myeloid Metaplasia (Myelofibrosis)
Polycythemia Vera
Essential Thrombocythemia
Phagocyte Disorders
Chediak-Higashi Syndrome
Chronic Granulomatous Disease
Neutrophil Actin Deficiency
Reticular Dysgenesis
Bone marrow cancers (Plasma Cell Disorders)
Multiple Myeloma
Plasma Cell Leukemia
Waldenstrom’s Macroglobulinemia
Transplants for Inherited Disorders effecting the Immune System & Other Organs
(all therapies are Allogeneic)
Cartilage-Hair Hypoplasia
Gunther’s Disease (Erythropoietic Porphyria)
Hermansky-Pudlak Syndrome
Pearson’s Syndrome
Shwachman-Diamond Syndrome
Systemic Mastocytosis
Transplants for Inherited Metabolic Disorders (all therapies are Allogeneic)
Mucopolysaccharidoses (MPS) Storage Diseases
Mucopolysaccharidoses (MPS)
Hurler’s Syndrome (MPS-IH)
Scheie Syndrome (MPS-IS)
Hunter’s Syndrome (MPS-II)
Sanfilippo Syndrome (MPS-III)
Morquio Syndrome (MPS-IV)
Maroteaux-Lamy Syndrome (MPS-VI)
Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
Mucolipidosis II (I-cell Disease)
Leukodystrophy Disorders
Adrenoleukodystrophy (ALD)/Adrenomyeloneuropathy (AMN)
Krabbe Disease (Globoid Cell Leukodystrophy)
Metachromatic Leukodystrophy
Pelizaeus-Merzbacher Disease
Lysosomal Storage Diseases
Gaucher Disease
Niemann-Pick Disease
Sandhoff Disease
Tay-Sachs Disease
Wolman Disease
Inherited Metabolic Disorders – Other
Lesch-Nyhan Syndrome (case report)
Osteopetrosis
Solid tumors not originating in the blood or immune system (Autologous therapy)
Neuroblastoma
Retinoblastoma